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GFI1

MIM.600871 1p22

Pathology

- germline mutations in GFI1 in congenital agranulocytosis

  • GFI1 product targets ELA2, encoding neutrophil elastase (NE)
  • ELA2 is mutated in autosomal recessive congenital agranulocytosis (Kostmann disease) and cyclic neutropenia